Study of nusinersen metabolites in the cerebrospinal fluid of children with spinal muscular atrophy using ultra-high-performance liquid chromatography coupled with quadrupole-time-of-flight mass spectrometry

Analyst, 2024, 149,3739-3746DOI: 10.1039/D4AN00436A, PaperSylwia Studzińska, Oliwia Błachowicz, Szymon Bocian, Oktawia Kalisz, Aleksandra Jaworska, Jakub Szymarek, Maria Mazurkiewicz-BełdzińskaThis study aimed to analyze nusinersen metabolites in cereb…